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Phase I: Complete Tumor Responses in MB

Baseline

Cycle 2

Cycle 3

11-year-old with recurrent

desmoplastic MB

372 mg/m

2

Treatment duration: 254 days

Baseline

Cycle 2

Cycle 5

4-year-old with recurrent

desmoplastic MB

425 mg/m

2

Treatment duration: 280 days